A Long-term Study for the Outcome of Pompe Disease

ConditionPompe Disease
Trial statusRecruiting
Trial phaseNot listed
Trial typeObservational
Biological sexAll
AgeNot listed
SponsorNational Taiwan University Hospital

About this trial

Prospectively follow patients with Pompe disease underwent enzyme replacement therapy.

Eligibility criteria

This trial does not accept healthy volunteers

Qualifiers

None

Disqualifiers

None

Trial population

Patients of Pompe disease who under enzyme replacement therapy

Trial design

Design model

Case-only

Time perspective

Prospective

Treatments tested in this trial

Not listed

Trial groups

No trial groups listed

Trial outcomes

Primary outcomes

1

all cause morbidities

Time frame
10 years

Secondary outcomes

Other outcomes

Sponsors and contacts

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