Exploratory Clinical Study on the Safety and Efficacy of Anti- CD19/BCMA U CAR-T Cell Injection for the Treatment of Relapsed/Refractory Autoimmune Diseases

Trial statusRecruiting
Trial phaseEarly Phase 1
Trial typeInterventional
Biological sexAll
Age18-70
SponsorChanghai Hospital

About this trial

A single arm, open-label pilot study is designed to determine the safety and effectiveness of anti-CD19/BCMA U CAR T cells in patients with autoimmune diseases.

60 patients are planned to be enrolled in the dose-escalation trial.

Eligibility criteria

This trial does not accept healthy volunteers

Qualifiers

Age: ≥ 18 years old and ≤ 70 years old, male or female;

Subject have previous diagnosis of systemic lupus erythematosus (SLE) (according to the 1997 American College of Rheumatology revised SLE classification criteria, the 2012 Systemic Lupus International Collaborating Clinics classification criteria, or the 2019 European League Against Rheumatism/American College of Rheumatology joint classification criteria);

Subjects had a modified SLEDAI-2K score of ≥8 at screening;

Subject has ≥ 1 organ system with BILAG-2004 Class A mobility score or ≥ 2 organ systems with BILAG-2004 Class B mobility score at screening;

Disqualifiers

Subjects with known severe allergic reactions, hypersensitivity, contraindication to any medications during the trial (cyclophosphamide, fludarabine, tozumabs), or subjects with a history of severe allergic reactions;

Existence or suspicion of uncontrollable or treatable fungal, bacterial, viral or other infections;

Subjects with central nervous system disorders caused by ADs or not caused by ADs (including epilepsy, psychiatric disorders, organic encephalopathy syndromes, cerebrovascular accidents, encephalitis, central nervous system vasculitis);

Subjects s with relatively serious heart diseases, such as angina pectoris, myocardial infarction, heart failure, and arrhythmia;

Trial design

Design model

Single group

Treatments tested in this trial

  • anti-CD19/BCMA U CAR T cells

    Biological/Vaccine

    Patients will receive Fludarabine and Cyclophosphamide on day-5, -4, and -3. Dose escalation will be performed for the single dose injection of anti-CD19/BCMA CAR T cells (KN3601)

Treatment groups

60 Participants
are divided into 1 treatment group
Group A: KN3601Experimental treatment 1 intervention

Trial outcomes

Primary outcomes

1

Incidence of Dose-Limiting Toxicity (DLT)

To characterize the safety of anti-CD19/BCMA U CAR T Cells (KN3601) for patients with Relapsed/Refractory autoimmune diseases

Time frame
up to 52 weeks after infusion
2

Incidence of Treatment Emergent Adverse Events (TEAEs)

To characterize the safety of anti-CD19/BCMA U CAR T Cells (KN3601) for patients with Relapsed/Refractory autoimmune diseases

Time frame
up to 52 weeks after infusion

Secondary outcomes

1

The overall response rate (ORR)

To characterize the efficacy of anti-CD19/BCMA U CAR T Cells (KN3601) for patients with Relapsed/Refractory autoimmune diseases

Time frame
up to 52 weeks after infusion
2

Disease control rate (DCR)

To characterize the efficacy of anti-CD19/BCMA U CAR T Cells (KN3601) for patients with Relapsed/Refractory autoimmune diseases

Time frame
up to 52 weeks after infusion
3

B cell depletion rate

To characterize the efficacy of anti-CD19/BCMA U CAR T Cells (KN3601) for patients with Relapsed/Refractory autoimmune diseases

Time frame
up to 52 weeks after infusion
4

B cell reconstitution

B cell subsets in peripheral blood measured by flow cytometry

Time frame
up to 52 weeks after infusion

Other outcomes

Sponsors and contacts

Click on the lead sponsor to view all of their trials.

Changhai Hospital

Lead sponsor

Rui Therapeutics Co., Ltd

Collaborator