POEM-F for Achalasia International Study

ConditionAchalasia
Trial statusRecruiting
Trial phaseNot applicable
Trial typeInterventional
Biological sexAll
Age18-65
SponsorChinese University of Hong Kong

About this trial

Per-oral endoscopic myotomy (POEM) has emerged as the endoscopic treatment of choice for achalasia, offering comparable symptom relief with laparoscopic Heller's cardiomyotomy. The main concern with POEM is the higher incidence of post-procedure gastroesophageal reflux disease (GERD), occurring in up to 50-60% of patients. In order to reduce the risk of GERD, endoscopic fundoplication has been developed as a novel procedure mimicking surgical anterior partial fundoplication that can be performed in the same session as POEM (POEM-F). Case series of POEM-F in patients with achalasia reported encouraging outcomes of low GERD rate of \~12% at 1 year. Prospective comparative data between POEM-F and conventional POEM on post-procedure GERD is current lacking. The investigators therefore designed an international multicenter prospective randomized study to investigate the efficacy of POEM-F. The investigators postulate that POEM-F could reduce the incidence of post-procedure GERD when compared with conventional POEM.

This is an international multicenter randomized controlled trial conducted between high volume expert centers from Hong Kong SAR, China, India and United States of America. Adult patients with manometry confirmed achalasia would be randomised to undergo POEM-F or POEM. The procedure would be performed by experts with vast experience in POEM. The primary outcome is the incidence of post-procedure GERD at 1 year, defined by the updated Lyon consensus. Secondary outcomes include technical and clinical success rates, adverse events, post-POEM endoscopic and manometry findings as well as patients' symptom scores.

Sample size calculation Based on existing pilot comparative data on POEM-F and POEM, it is estimated that 84 patients would be required to demonstrate a difference in post-procedure GERD of 47.6% to 18.2%, with 80% power and false positive rate of 0.05, accounting for 10% loss to follow-up.

Purpose and potential The current study proposal could demonstrate the superiority of POEM-F over POEM in reducing post-procedural GERD. It would also demonstrate the safety and reproducibility of the technique in expert centers across the globe. It could potentially replace conventional POEM as the preferred minimally invasive endoscopic treatment for achalasia.

Eligibility criteria

This trial does not accept healthy volunteers

Qualifiers

Adult patient (age ≥18 and ≤65 years-old) and with symptomatic achalasia type I or II.

Capability of understanding and complying with the study requirements, including filling the Eckardt Score, GERD-HRQL and RSI questionnaire and signing the informed consent form.

Treatment naïve, or

Failed prior through-the-scope balloon dilation, Savary or pneumatic dilation

Disqualifiers

Patients unable or unwilling to provide consent.

Previous esophageal or gastric surgery.

Prior achalasia treatment including Heller myotomy, POEM.

Sigmoid achalasia, or significant esophageal dilatation >6cm in lower esophagus

Trial design

Design model

Parallel

Treatments tested in this trial

  • POEM-F

    Procedure/Surgery

    POEM-F would be performed as described in the arms section

  • Conventional POEM

    Procedure/Surgery

    Anterior POEM performed as described in the arms section

Treatment groups

81 Participants
are divided into 2 treatment groups
Group A: Per-oral endoscopic myotomy with fundoplicationExperimental treatment 1 intervention
Group B: Conventional POEMActive comparator 1 intervention

Trial outcomes

Primary outcomes

1

Post-procedure rate of gastroesophageal reflux

Defined by updated Lyon 2.0 consensus as fulfilling one or more of the criteria: 1. Endoscopic erosive esophagitis, LA grade B or above 2. Long segment Barrett's esophagus 3. Peptic esophageal stricture 4. 24-hour pH study with acid exposure time \>6% Both endoscopy and pH study to be performed with proton pump inhibitor stopped for 4 weeks

Time frame
1 year

Secondary outcomes

1

Clinical success rate of procedure

Post-treatment Eckhardt score \<=3

Time frame
1 year
2

Adverse event of procedure

frequency of severe adverse events with probable or definite attribution to the procedure based on the American Society of Gastrointestinal Endoscopy (ASGE) lexicon as well as Clavien Dindo classification

Time frame
30 day
3

Technical success rate of procedure

Completing all steps of the intended procedure successfully in the same session

Time frame
1 day
4

Procedure time

Procedure time of the intended procedure in minutes

Time frame
1 day

Other outcomes

Sponsors and contacts

Click on the lead sponsor to view all of their trials.

Chinese University of Hong Kong

Lead sponsor

Deenanath Mangeshkar Hospital and Research Centre

Collaborator

Johns Hopkins University

Collaborator

Northwestern University

Collaborator

Nanfang Hospital, Southern Medical University

Collaborator

Asian Institute of Gastroenterology, India

Collaborator

Post Graduate Institute of Medical Education and Research, Chandigarh

Collaborator