Prospective Clinical Assessment Study in Children With Hypochondroplasia
ConditionHypochondroplasia
Trial statusRecruiting
Trial phaseNot listed
Trial typeObservational
Biological sexAll
Age30-16
SponsorQED Therapeutics, a BridgeBio company
About this trial
This is a long-term, multicenter, non-interventional study of children ages 2.5 to \<17 years with hypochondroplasia (HCH).
Eligibility criteria
This trial does not accept healthy volunteersQualifiers
None
Disqualifiers
None
Trial population
Children with hypochondroplasia
Trial design
Design model
Case-only
Time perspective
Prospective
Treatments tested in this trial
Not listed
Trial groups
No trial groups listed
Trial outcomes
Primary outcomes
1
Annualized height velocity
Time frame
up to 3 yearsSecondary outcomes
1
Change over time in height Z-score, upper arm to forearm ratio, and upper leg to lower leg ratio
Time frame
up to 3 years2
Cognitive functions
Time frame
up to 3 years3
HCH-related medical events reported as medical history or NT-AEs
Time frame
up to 3 years4
HCH-related surgical procedures
Time frame
up to 3 yearsOther outcomes
1
Change from BL in collagen X marker concentration (ug/L).
Time frame
up to 3 yearsSponsors and contacts
Click on the lead sponsor to view all of their trials.
Source ClinicalTrials.gov