The World Federation of Hemophilia Gene Therapy Registry
ConditionHemophilia
Trial statusNot yet recruiting
Trial phaseNot listed
Trial typeObservational
Biological sexAll
Age0-100
SponsorWorld Federation of Hemophilia
About this trial
The aim of the WFH GTR is to provide a database in which long-term data on PWH who receive gene therapy from around the world, will be collected and housed.
Eligibility criteria
This trial does not accept healthy volunteersQualifiers
People with hemophilia who have received a gene therapy product
Disqualifiers
None
Trial population
All people with hemophilia who have received a gene therapy product
Trial design
Design model
Cohort
Time perspective
Prospective
Treatments tested in this trial
Gene therapy
Other interventionThis is a prospective patient registry.
Treatment groups
No treatment groups listed
Trial outcomes
Primary outcomes
1
Change in long term safety: adverse events of interest
Months 3, 6, 9, 12, 18, 24; and annually thereafter for 15 years.
Time frame
From baseline, through study completion (15 years)2
Change in efficacy: factor level and bleeding events
Months 3, 6, 9, 12, 18, 24; and annually thereafter for 15 years.
Time frame
From baseline, through study completion (15 years)Locations
Sponsors and contacts
Click on the lead sponsor to view all of their trials.
Source ClinicalTrials.gov
This trial is not recruiting at the moment. You can still explore other options: