Dystrophinopathies

1

Review clinical trials related to Dystrophinopathies. Use filters to narrow results by trial status, phase, treatment, biological sex and sponsor.

Condition / disease
Location
Status: Recruiting

Decoding Central Defects in Dystrophinopathies From Diagnostic to Remediation

The study aims to identify a genotype/phenotype correlation by analyzing more finely the neurodevelopmental disorders in DMD patients.

Participants needed: 110
Trial details
Age: 5-12Biological sex: AllType: ObservationalSponsor: Assistance Publique - Hôpitaux de ParisUpdated: Sep 22, 2026Locations: 1
Eligibility criteria

French citizenship, affiliated to the French Social Security, [+3]

Severe intellectual deficiency with IQ < 55, and IQ < 70 for the deep neurocogni... [+6]