Multiple Acyl-CoA Dehydrogenase Deficiency

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Review clinical trials related to Multiple Acyl-CoA Dehydrogenase Deficiency. Use filters to narrow results by trial status, phase, treatment, biological sex and sponsor.

Condition / disease
Location
Status: Not yet recruiting

Natural History of MADD

The objective of this study is to conduct a longitudinal, observational investigation to determine the natural history of Multiple Acyl-CoA Dehydrogenase Deficiency (MADD), delineate the spectrum of its clinical features and their progression, identify biomarkers, and develop and validate patient reported outcomes.

Participants needed: 50
Trial details
Biological sex: AllType: ObservationalSponsor: Icahn School of Medicine at Mount SinaiUpdated: Jul 29, 2026Locations: 2Duration: 5 Years
Eligibility criteria

Have a biochemical and/or molecular diagnosis of Multiple Acyl-CoA Dehydrogenase... [+1]