Review clinical trials related to Sly Syndrome. Use filters to narrow results by trial status, phase, treatment, biological sex and sponsor.
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The objectives of this study are to characterize MPS VII disease presentation and progression and assess long-term effectiveness and safety, including hypersensitivity reactions and immunogenicity of vestronidase alfa.
Diagnosis of MPS VII based on laboratory diagnosis, including either enzymatic o... [+2]
Concurrent participation in other pharmaceutical company-sponsored interventiona...