Health Trials

Clinical trials

2

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Condition / disease
Location
Status: Recruiting

A Study to Evaluate the Efficacy and Safety of Subcutaneous Nomlabofusp in Subjects With Friedreich's Ataxia

To evaluate the efficacy and safety of subcutaneous nomlabofusp in adult and pediatric subjects with Friedreich's ataxia

Participants needed: 150
Trial details
Phase: Phase 3Age: 12-40Biological sex: AllType: InterventionalSponsor: Larimar Therapeutics, Inc.Updated: Aug 21, 2026Locations: 3
Eligibility criteria

Subject must provide genetically confirmed FRDA diagnosis report and is homozygo... [+8]

Subject who is confirmed as compound heterozygous (GAA repeat expansion on only... [+13]

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Status: Recruiting

An Open-Label Study of CTI-1601 in Subjects With Friedreich's Ataxia

An open label study designed to evaluate the safety, PK, PD, and clinical effects of long-term daily administration of CTI-1601 enrolling adolescent and adult patients with FRDA who have participated in a prior clinical study of CTI-1601 as well as children (age 2 years and older), adolescents and adults with FRDA who have not participated in a prior clinical study of CTI-1601.

Participants needed: 85
Trial details
Phase: Phase 2Age: 2-60Biological sex: AllType: InterventionalSponsor: Larimar Therapeutics, Inc.Updated: May 13, 2026Locations: 8
Eligibility criteria

Subjects with FRDA who have or have not previously completed participation in a... [+2]

Subjects who are confirmed as compound heterozygous (GAA repeat expansion on onl... [+10]

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