Status: Recruiting
Study to Evaluate Biological & Clinical Effects of Significantly Corrected CFTR Function in Infants & Young Children
This is a two-part, multi-center, prospective longitudinal, exploratory study of highly effective cystic fibrosis transmembrane conductance regulator (CFTR) modulators and their impact on children with cystic fibrosis (CF).
Participants needed: 210
Trial details
Age: Up to 10Biological sex: AllType: ObservationalSponsor: Sonya HeltsheUpdated: Jul 8, 2026Locations: 35
Eligibility criteria
Less than 10 years of age at the first study visit. [+5]
Use of an investigational drug within 28 days prior to and including the first s... [+2]