Status: Recruiting
Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP)
This LTFU is being conducted to assess long-term safety and durability of response in participants dosed with IP in a parent protocol, and to collect longitudinal natural history in enrolled but not dosed participants who also participated in a parent protocol.
Participants needed: 13
Trial details
Age: 7-15Biological sex: AllType: ObservationalSponsor: iECURE, Inc.Updated: Aug 31, 2026Locations: 3
Eligibility criteria
Enrolled in an iECURE parent protocol and have either completed or discontinued... [+2]